Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, and Advocacy

Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, ...
Medical Xpress

Nervous System Diseases: News and Research on Muscular Diseases

In a new discovery, chronic pain has been shown to be physiologically different from acute pain and now scientists have the roadmap for how to target it. While many people with neuromuscular diseases ...
Business Insider

Muscular Dystrophy Association Announces nearly $2 Million in Collaborative Research Grants Advancing Treatments Across Multiple Neuromuscular Diseases

New York, Dec. 03, 2025 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) today announced the awarding of seven new collaborative research grants totaling nearly $2 million to advance ...
Nasdaq

Capricor Therapeutics Receives Orphan Drug Designation for Deramiocel in Becker Muscular Dystrophy, Expanding Focus in Neuromuscular Diseases

Capricor Therapeutics announced that the U.S. FDA has granted Orphan Drug Designation to its lead cell therapy candidate, Deramiocel, for the treatment of Becker Muscular Dystrophy (BMD). This ...
EurekAlert!

Genethon signs licensing agreement with AskBio for the development of an investigational gene therapy for Pompe disease

Genethon, a leading laboratory in gene therapy for rare diseases, today announced that it has entered into an exclusive, worldwide licensing agreement with AskBio, a gene therapy company wholly owned ...
Medical Xpress

Nervous System Diseases: News and Research on Muscular Diseases

A systematic review of research spanning 34 years has found a biological link between two common neurological conditions that can potentially save the NHS millions by streamlining treatments that ...